Clinical Trials in Rare Diseases - General Resources
Batten Disease Resources and Links
Here we provide some general resources relevant to clinical trials in rare diseases, including a list of relevant articles and website links. Please note that we cannot directly post published articles, due to copyright laws. However, wherever available, we have provided a link to a free, downloadable version of the article. Please contact us if you wish to suggest other materials to be shared here.
Support for this conference was provided by:
The National Institutes of Health – National Institute of Neurological Diseases and Stroke (NIH/NINDS): 1R13 NS078981,
Outcomes and Infrastructure for Phase III Clinical Trials in JNCL - Batten Disease
The University of Rochester Child Neurology Research Fund