Tag: muscular dystrophy

New funding will extend URMC's key role in national research network just a new gene therapies or neuromuscular and other disorders are emerging.

Emma Ciafaloni, MD, describes how the new drug works, why the FDA chose to limit its use, and what it means for patients and their families.

Since April 2015, Nicholas O’Neill has traveled nearly three hours by car every week from southeast of Syracuse to Golisano Children’s Hospital. Here, in the confines of the Clinical Research Center, ...