Strong Kids

Researchers receive grant to study gene therapy and DNA delivery

Dec. 5, 2014

Cell illustrationSince its discovery several decades ago, gene therapy has been a medicinal sphinx, with doctors as enamored by its potential as they are frustrated by the riddles it presents.

Researchers at the University of Rochester Medical Center are working to solve one of those riddles.

In order for gene therapy to be effective, doctors must discern how to deliver DNA to a cell’s nucleus, which requires a comprehensive understanding of how DNA and proteins move through cell cytoplasm. Knowledge of this system could lead to huge leaps in gene therapy effectiveness, and could potentially allow researchers to push forward on research into many currently-untreatable diseases.