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Pediatric Research News

New Gene Therapy Poised to Transform Care for Spinal Muscular Atrophy

Jun 05, 2019

The University of Rochester Medical Center has been tapped as one of the first institutions in the U.S. to offer a new gene replacement therapy to treat spinal muscular atrophy. The new treatment, which is being marketed by Novartis under the brand name Zolgensma, can be delivered within weeks of birth and clinical trials have shown that it dramatically changes the course of the disease.

Dyson Day Lecture Lecture to Unveil Results of Literacy Program in RCSD

Mar 06, 2019

Students in the Rochester City School District enrolled in a new literacy program showed twice as much progress as their peers, according to a recent study by Carol St. George, Ed.D., associate professor and director of the literacy education program at the University of Rochester’s Warner School.


URMC Pediatrics Research Newsletter